We focus Rare disorders
Neurology disorders
LNS
TSC
LHON
Blood Disorders
PNH
MDS
kidney Rare
C3
FSGS
MN
Connect to research for your rare
Paroxysmal nocturnal hemoglobinuria (PNH)
PNH natural history database
PNH Clinical trial
Lesch-Nyhan syndrome
LNS natural history database
LNS Clinical trial
C3 glomerulopathy
C3G natural history database
C3G Clinical trial
How it works
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PNH patients
SEQUENCING
symptoms
ANALYSIS
test results
DISCUSSION
Experts cousult