We connect care givers focus your rare

We focus Rare disorders

Neurology disorders

LNS

TSC

LHON

Blood Disorders

PNH

MDS

 

kidney Rare

C3

FSGS

MN

 

Connect to research for your rare

Paroxysmal nocturnal hemoglobinuria (PNH)

PNH natural history database

PNH Clinical trial

Lesch-Nyhan syndrome

LNS natural history database

LNS  Clinical trial

C3 glomerulopathy

C3G natural history database

C3G Clinical trial

How it works

REGISTER

PNH patients

SEQUENCING

symptoms

ANALYSIS

test results

DISCUSSION

Experts cousult

Contact

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